Health and Me on MSN12h
These Are The Five Rare Diseases You Did Not Know Existed
It is always good to know about diseases so you can read the signs your body is telling you. However, there exists many ...
Their flesh turns to bone, but a new treatment might help them
That is the predicament of patients with fibrodysplasia ossificans progressiva (FOP) or “Stone Man Syndrome”, a rare ...
Chip Chick on MSN12d
Stone Man Syndrome Is A Rare Disease That Turns Muscles Into Bones
For patients with a rare genetic disorder that turns their muscles into bone, there is new hope. The disease is […] ...
Nature2y
Landmark study completed for ultra-rare bone-forming disease
Early diagnosis is essential for a child with FOP, but this has rarely been easy. The symptoms can easily be mistaken for those of other diseases; FOP is ultra-rare, affecting only one in 1.4 ...
pharmaphorum1y
Ipsen drug is first therapy for rare bone disease FOP in US
Previously, the only therapy available to patients with FOP was medicines to treat symptoms, including pain. Palovarotene was acquired by Ipsen as part of its $1 billion upfront acquisition of ...
pharmaphorum2y
Ipsen's rare disease drug palovarotene knocked back in EU
At the moment, the only therapy available to patients with FOP – a disorder in which bony lesions are laid down in muscles, tendons, and ligaments – are drugs to treat symptoms including pain.