Data from the phase 2 ROME trial were presented by Andrea Botticelli, MD, during the ESMO Targeted Anticancer Therapies ...

Thyroid cancer-associated syndromes, including multiple endocrine neoplasia type 2, were significantly more prevalent than current estimates.

PATTERSON-UTI ENERGY insiders have traded $PTEN stock on the open market 5 times in the past 6 months. Of those trades, 1 have been purchases and 4 have been sales ...

A baby born with a rare and dangerous genetic disease is growing and thriving after getting an experimental gene editing treatment made just for him. Researchers described the case in a new study ...

The one-off treatment highlights the promise of a new type of gene editing and the challenges of using it to treat extremely rare genetic diseases. Doctors say they constructed a bespoke gene ...

A baby born with a rare and dangerous genetic disease is growing and thriving after getting an experimental gene editing treatment made just for him. The baby, KJ Muldoon of Clifton Heights ...

A flexible, intrinsically disordered region (IDR) in the TAF2 protein directs its movement between gene promoters and nuclear speckles, linking transcription initiation and RNA processing.

You can reach Jason on Signal at JasonMast.05. NEW ORLEANS — The mood at the annual meeting of the American Society of Cell and Gene Therapy isn’t amazing. The biotech market has been bad for ...

Instead, at 6 months, doctors administered the first dose of the gene editing treatment. They have since been able to loosen a strict low-protein diet and reduce his daily ammonia-lowering ...

Scientists present current evidence for a new gene therapy for Duchenne muscular dystrophy called delandistrogene moxeparvovec. AAN Evidence in Focus articles highlight the strength of the current ...

May 15, 2025 — A research team has developed and safely delivered a personalized gene editing therapy to treat an infant with a life-threatening, incurable genetic disease. The infant ...